MUMBAI, India, Aug. 17 -- Intellectual Property India has published a patent application (202618079320 A) filed by Research Institute At Nationwide Children'S Hospital on June 26, 2026, for Adeno-Associated Virus Vector Delivery Of Muscle Specific Micro-Dystrophin To Treat Muscular Dystrophy.
Inventors include Rodino-Klapac, Louise; and Mendell, Jerry, R..
The application for the patent was published on August 14, 2026, under issue no. 33/2026.
Abstract: ABSTRACT ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MUSCLE SPECIFIC MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY The invention provides gene therapy vectors, such as adeno-associated virus (AAV) vectors, 5 expressing a miniaturized human micro-dystrophin gene and method of using these vectors to express micro-dystrophin in skeletal muscle s including diaphragm and cardiac muscle and to protect muscle fibers from injury, increase muscle strength and reduce and/or prevent fibrosis in subjects suffering from muscular dystrophy. 10 45
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